Reach more patients at the right time.
Rare Disease
A rare disease shouldn't mean years without answers.
We wait years for a diagnosis and the right care.
The burden
30 million
people in the U.S. have a rare disease, nearly 10% of the population1
3–15 years
is a common timeline for a rare disease diagnosis1
95%
of rare diseases lack an FDA-approved treatment1
Sources
- National Center for Advancing Translational Sciences (NIH). Rare Diseases Fact Sheet. 2023.
Figures as stated by each source; checked November 2026.
Key dates in Rare Disease
Moments to act together.
Next six months. Dates from official sites; checked November 2026. Programs run in the United States. Global congresses and world days are listed for reference.
Work with us in Rare Disease
Patients can't wait. Neither can we.
Publish measurable improvement in patient care.
Close the gap between eligible patients and guideline-based care.
What's new in Rare Disease
How care is changing.
Updated weekly from federal agencies, guideline bodies and national nonprofits. U.S. sources for now, while programs run in the United States. Approvals are listed by date from FDA notices. Rabble Health may work with companies whose products appear here; no company reviews or influences what is listed.
Talk to us
Bring us a care gap.
Tell us where patients are falling out of care.
connect@rabblehealth.com